Main Outcome Measure(s)
Publication stageIn Press Accepted Manuscript
Funding Statement: No funding was obtained for this study.
Disclosure Statement: PJO, AOG, and TCL are investigators on the Leni-D gene therapy trial sponsored by bluebird bio to treat patients with cerebral adrenoleukodystrophy.
Attestation Statement: The subjects in this trial have not concomitantly been involved in other randomized trials. Data regarding any of the subjects in the study has not been previously published unless specified. Data will be made available to the editors of the journal for review or query upon request.
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